Project Grant R03TR004848

Award Date 6/15/25
Completion Date 6/14/26
Dollars Obligated $178K
Federal Grant Program
93.350
Assistance Type
Project Grant
Place of Performance
Massachusetts, USA
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This federal Project Grant award from the National Center for Advancing Translational Sciences (NCATS), CFDA 93.350, will fund research to develop a treatment for Familial Platelet Disorder with Myeloid Malignancy (FPDMM), a rare genetic disorder affecting hundreds of people in the U.S. The $489,500 award to The Children's Hospital of Philadelphia will support studies on the small compound Repsox, which has shown promise in correcting the platelet defects and reducing leukemia risk in FPDMM. The...
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